AAV1-hOTOF gene therapy for autosomal recessive deafness 9: a single-arm trial

Lv, Jun ; Wang, Hui ; Cheng, Xiaoting ; Chen, Yuxin ; Wang, Daqi ; Zhang, Longlong ; Cao, Qi ; Tang, Honghai ; Hu, Shaowei ; Gao, Kaiyu ; Xun, Mengzhao ; Wang, Jinghan ; Wang, Zijing ; Zhu, Biyun ; Cui, Chong ; Gao, Ziwen ; Guo, Luo ; Yu, Sha ; Jiang, Luoying ; Yin, Yanbo ; Zhang, Jiajia ; Chen, Bing ; Wang, Wuqing ; Chai, Renjie ; Chen, Zheng-Yi ; Li, Huawei ; Shu, Yilai

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England: Elsevier Ltd

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