Gene therapy for mucopolysaccharidoses: in vivo and ex vivo approaches
Fraldi, Alessandro ; Serafini, Marta ; Sorrentino, Nicolina Cristina ; Gentner, Bernhard ; Aiuti, Alessandro ; Bernardo, Maria Ester
Italian journal of pediatrics, 2018-11, Vol.44 (Suppl 2), p.130-130, Article 130 [Periódico revisado por pares]England: BioMed Central
Texto completo disponível