Targeting neuronal lysosomal dysfunction caused by β-glucocerebrosidase deficiency with an enzyme-based brain shuttle construct

Gehrlein, Alexandra ; Udayar, Vinod ; Anastasi, Nadia ; Morella, Martino L ; Ruf, Iris ; Brugger, Doris ; von der Mark, Sophia ; Thoma, Ralf ; Rufer, Arne ; Heer, Dominik ; Pfahler, Nina ; Jochner, Anton ; Niewoehner, Jens ; Wolf, Luise ; Fueth, Matthias ; Ebeling, Martin ; Villaseñor, Roberto ; Zhu, Yanping ; Deen, Matthew C ; Shan, Xiaoyang ; Ehsaei, Zahra ; Taylor, Verdon ; Sidransky, Ellen ; Vocadlo, David J ; Freskgård, Per-Ola ; Jagasia, Ravi

Nature communications, 2023-04, Vol.14 (1), p.2057-2057, Article 2057 [Periódico revisado por pares]

England: Nature Publishing Group

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