Two-Year Outcomes of Valoctocogene Roxaparvovec Therapy for Hemophilia A

Mahlangu, Johnny ; Kaczmarek, Radoslaw ; von Drygalski, Annette ; Shapiro, Susan ; Chou, Sheng-Chieh ; Ozelo, Margareth C. ; Kenet, Gili ; Peyvandi, Flora ; Wang, Michael ; Madan, Bella ; Key, Nigel S. ; Laffan, Michael ; Dunn, Amy L. ; Mason, Jane ; Quon, Doris V. ; Symington, Emily ; Leavitt, Andrew D. ; Oldenburg, Johannes ; Chambost, Hervé ; Reding, Mark T. ; Jayaram, Kala ; Yu, Hua ; Mahajan, Reena ; Chavele, Konstantia-Maria ; Reddy, Divya B. ; Henshaw, Joshua ; Robinson, Tara M. ; Wong, Wing Yen ; Pipe, Steven W.

The New England journal of medicine, 2023-02, Vol.388 (8), p.694-705 [Periódico revisado por pares]

United States: Massachusetts Medical Society

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