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1 |
Material Type: Artigo
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Phase 1 Trial of an RNA Interference Therapy for Acute Intermittent PorphyriaSardh, Eliane ; Harper, Pauline ; Balwani, Manisha ; Stein, Penelope ; Rees, David ; Bissell, D. Montgomery ; Desnick, Robert ; Parker, Charles ; Phillips, John ; Bonkovsky, Herbert L ; Vassiliou, Daphne ; Penz, Craig ; Chan-Daniels, Amy ; He, Qiuling ; Querbes, William ; Fitzgerald, Kevin ; Kim, Jae B ; Garg, Pushkal ; Vaishnaw, Akshay ; Simon, Amy R ; Anderson, Karl EThe New England journal of medicine, 2019-02, Vol.380 (6), p.549-558 [Periódico revisado por pares]United States: Massachusetts Medical SocietyTexto completo disponível |
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Material Type: Artigo
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PorphyriaBissell, D. Montgomery ; Anderson, Karl E ; Bonkovsky, Herbert L Longo, Dan L ; Longo, Dan L.The New England journal of medicine, 2017-08, Vol.377 (9), p.862-872 [Periódico revisado por pares]United States: Massachusetts Medical SocietyTexto completo disponível |
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Material Type: Artigo
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Acute Porphyrias in the USA: Features of 108 Subjects from Porphyrias ConsortiumBonkovsky, Herbert L., MD ; Maddukuri, Vinaya C., MD ; Yazici, Cemal, MD ; Anderson, Karl E., MD ; Bissell, D. Montgomery, MD ; Bloomer, Joseph R., MD ; Phillips, John D., PhD ; Naik, Hetanshi, MSc ; Peter, Inga, PhD ; Baillargeon, Gwen, MSc ; Bossi, Krista, MSc ; Gandolfo, Laura, MSc ; Light, Carrie, MSc ; Bishop, David, PhD ; Desnick, Robert J., MD, PhDThe American journal of medicine, 2014-12, Vol.127 (12), p.1233-1241 [Periódico revisado por pares]United States: Elsevier IncTexto completo disponível |
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Material Type: Artigo
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Role of Delta-aminolevulinic Acid in the Symptoms of Acute PorphyriaBissell, D. Montgomery, MD ; Lai, Jennifer C., MD ; Meister, Raymond K., MD, MPH ; Blanc, Paul D., MD, MSPHThe American journal of medicine, 2015-03, Vol.128 (3), p.313-317 [Periódico revisado por pares]United States: Elsevier IncTexto completo disponível |
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Material Type: Artigo
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Information from pharmaceutical companies and the quality, quantity, and cost of physicians' prescribing: a systematic reviewSpurling, Geoffrey K ; Mansfield, Peter R ; Montgomery, Brett D ; Lexchin, Joel ; Doust, Jenny ; Othman, Noordin ; Vitry, Agnes I Henry, DavidPLoS medicine, 2010-10, Vol.7 (10), p.e1000352-e1000352 [Periódico revisado por pares]United States: Public Library of ScienceTexto completo disponível |
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Material Type: Artigo
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Dersimelagon in Erythropoietic ProtoporphyriasBalwani, Manisha ; Bonkovsky, Herbert L. ; Levy, Cynthia ; Anderson, Karl E. ; Bissell, D. Montgomery ; Parker, Charles ; Takahashi, Fumihiro ; Desnick, Robert J. ; Belongie, KirstineThe New England journal of medicine, 2023-04, Vol.388 (15), p.1376-1385 [Periódico revisado por pares]United States: Massachusetts Medical SocietyTexto completo disponível |
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Material Type: Artigo
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Waldenström macroglobulinemia with secondary pure red cell aplasia in a patient with metastatic castrate resistant prostate cancer receiving an immune checkpoint inhibitor: a case reportKumar, Vaibhav ; Montgomery, Nathan D ; van Deventer, Hendrik W ; Whang, Young EJournal of medical case reports, 2023-05, Vol.17 (1), p.220-220, Article 220 [Periódico revisado por pares]England: BioMed Central LtdTexto completo disponível |
8 |
Material Type: Artigo
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PorphyriaSood, Siddharth ; Mingos, Nicholas ; Ross, Gayle ; Jaramillo-Calle, Daniel A ; Bissell, D. Montgomery ; Anderson, Karl E ; Bonkovsky, Herbert LThe New England journal of medicine, 2017-11, Vol.377 (21), p.2100-2101 [Periódico revisado por pares]United States: Massachusetts Medical SocietyTexto completo disponível |
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Material Type: Artigo
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Afamelanotide for Erythropoietic ProtoporphyriaLangendonk, Janneke G ; Balwani, Manisha ; Anderson, Karl E ; Bonkovsky, Herbert L ; Anstey, Alexander V ; Bissell, D. Montgomery ; Bloomer, Joseph ; Edwards, Chris ; Neumann, Norbert J ; Parker, Charles ; Phillips, John D ; Lim, Henry W ; Hamzavi, Iltefat ; Deybach, Jean-Charles ; Kauppinen, Raili ; Rhodes, Lesley E ; Frank, Jorge ; Murphy, Gillian M ; Karstens, Francois P.J ; Sijbrands, Eric J.G ; de Rooij, Felix W.M ; Lebwohl, Mark ; Naik, Hetanshi ; Goding, Colin R ; Wilson, J.H. Paul ; Desnick, Robert JThe New England journal of medicine, 2015-07, Vol.373 (1), p.48-59 [Periódico revisado por pares]United States: Massachusetts Medical SocietyTexto completo disponível |
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Material Type: Artigo
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Multicentric Castleman's disease in MalawiGopal, Satish, Dr ; Fedoriw, Yuri, MD ; Montgomery, Nathan D, MD ; Kampani, Coxcilly, Dip ; Krysiak, Robert, MS ; Sanders, Marcia K, BS ; Dittmer, Dirk P, PhD ; Liomba, N George, FRCPathThe Lancet (British edition), 2014-09, Vol.384 (9948), p.1158-1158 [Periódico revisado por pares]Kidlington: Elsevier LtdTexto completo disponível |