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1 |
Material Type: Artigo
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Juvenile myelomonocytic leukemia: who's the driver at the wheel?Niemeyer, Charlotte M. ; Flotho, ChristianBlood, 2019-03, Vol.133 (10), p.1060-1070 [Periódico revisado por pares]United States: Elsevier IncTexto completo disponível |
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Material Type: Artigo
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How I treat juvenile myelomonocytic leukemiaLocatelli, Franco ; Niemeyer, Charlotte M.Blood, 2015-02, Vol.125 (7), p.1083-1090 [Periódico revisado por pares]United States: Elsevier IncTexto completo disponível |
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Material Type: Artigo
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An international consortium proposal of uniform response criteria for myelodysplastic/myeloproliferative neoplasms (MDS/MPN) in adultsSavona, Michael R. ; Malcovati, Luca ; Komrokji, Rami ; Tiu, Ramon V. ; Mughal, Tariq I. ; Orazi, Attilio ; Kiladjian, Jean-Jacques ; Padron, Eric ; Solary, Eric ; Tibes, Raoul ; Itzykson, Raphael ; Cazzola, Mario ; Mesa, Ruben ; Maciejewski, Jaroslaw ; Fenaux, Pierre ; Garcia-Manero, Guillermo ; Gerds, Aaron ; Sanz, Guillermo ; Niemeyer, Charlotte M. ; Cervantes, Francisco ; Germing, Ulrich ; Cross, Nicholas C.P. ; List, Alan F.Blood, 2015-03, Vol.125 (12), p.1857-1865 [Periódico revisado por pares]United States: Elsevier IncTexto completo disponível |
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Material Type: Artigo
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Classification of childhood aplastic anemia and myelodysplastic syndromeNiemeyer, Charlotte M ; Baumann, IrithHematology, 2011, Vol.2011 (1), p.84-89United StatesTexto completo disponível |
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Material Type: Artigo
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Mutations in CBL occur frequently in juvenile myelomonocytic leukemiaLoh, Mignon L. ; Sakai, Debbie S. ; Flotho, Christian ; Kang, Michelle ; Fliegauf, Manfred ; Archambeault, Sophie ; Mullighan, Charles G. ; Chen, Leslie ; Bergstraesser, Eva ; Bueso-Ramos, Carlos E. ; Emanuel, Peter D. ; Hasle, Henrik ; Issa, Jean-Pierre ; van den Heuvel-Eibrink, Marry M. ; Locatelli, Franco ; Starý, Jan ; Trebo, Monica ; Wlodarski, Marcin ; Zecca, Marco ; Shannon, Kevin M. ; Niemeyer, Charlotte M.Blood, 2009-08, Vol.114 (9), p.1859-1863 [Periódico revisado por pares]Washington, DC: Elsevier IncTexto completo disponível |
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Material Type: Artigo
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Congenital sideroblastic anemia due to mutations in the mitochondrial HSP70 homologue HSPA9Schmitz-Abe, Klaus ; Ciesielski, Szymon J. ; Schmidt, Paul J. ; Campagna, Dean R. ; Rahimov, Fedik ; Schilke, Brenda A. ; Cuijpers, Marloes ; Rieneck, Klaus ; Lausen, Birgitte ; Linenberger, Michael L. ; Sendamarai, Anoop K. ; Guo, Chaoshe ; Hofmann, Inga ; Newburger, Peter E. ; Matthews, Dana ; Shimamura, Akiko ; Snijders, Pieter J.L.M. ; Towne, Meghan C. ; Niemeyer, Charlotte M. ; Watson, Henry G. ; Dziegiel, Morten H. ; Heeney, Matthew M. ; May, Alison ; Bottomley, Sylvia S. ; Swinkels, Dorine W. ; Markianos, Kyriacos ; Craig, Elizabeth A. ; Fleming, Mark D.Blood, 2015-12, Vol.126 (25), p.2734-2738 [Periódico revisado por pares]United States: Elsevier IncTexto completo disponível |
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Material Type: Artigo
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A recurring mutation in the respiratory complex 1 protein NDUFB11 is responsible for a novel form of X-linked sideroblastic anemiaLichtenstein, Daniel A. ; Crispin, Andrew W. ; Sendamarai, Anoop K. ; Campagna, Dean R. ; Schmitz-Abe, Klaus ; Sousa, Cristovao M. ; Kafina, Martin D. ; Schmidt, Paul J. ; Niemeyer, Charlotte M. ; Porter, John ; May, Alison ; Patnaik, Mrinal M. ; Heeney, Matthew M. ; Kimmelman, Alec ; Bottomley, Sylvia S. ; Paw, Barry H. ; Markianos, Kyriacos ; Fleming, Mark D.Blood, 2016-10, Vol.128 (15), p.1913-1917 [Periódico revisado por pares]United States: Elsevier IncTexto completo disponível |
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Material Type: Artigo
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Comparison of the efficacy of rabbit and horse antithymocyte globulin for the treatment of severe aplastic anemia in childrenYoshimi, Ayami ; Niemeyer, Charlotte M. ; Führer, Monika M. ; Strahm, BrigitteBlood, 2013-01, Vol.121 (5), p.860-861 [Periódico revisado por pares]United States: Elsevier IncTexto completo disponível |
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9 |
Material Type: Artigo
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Prevalence, clinical characteristics, and prognosis of GATA2-related myelodysplastic syndromes in children and adolescentsWlodarski, Marcin W. ; Hirabayashi, Shinsuke ; Pastor, Victor ; Starý, Jan ; Hasle, Henrik ; Masetti, Riccardo ; Dworzak, Michael ; Schmugge, Markus ; van den Heuvel-Eibrink, Marry ; Ussowicz, Marek ; De Moerloose, Barbara ; Catala, Albert ; Smith, Owen P. ; Sedlacek, Petr ; Lankester, Arjan C. ; Zecca, Marco ; Bordon, Victoria ; Matthes-Martin, Susanne ; Abrahamsson, Jonas ; Kühl, Jörn Sven ; Sykora, Karl-Walter ; Albert, Michael H. ; Przychodzien, Bartlomiej ; Maciejewski, Jaroslaw P. ; Schwarz, Stephan ; Göhring, Gudrun ; Schlegelberger, Brigitte ; Cseh, Annámaria ; Noellke, Peter ; Yoshimi, Ayami ; Locatelli, Franco ; Baumann, Irith ; Strahm, Brigitte ; Niemeyer, Charlotte M.Blood, 2016-03, Vol.127 (11), p.1387-1397 [Periódico revisado por pares]United States: Elsevier IncTexto completo disponível |
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10 |
Material Type: Artigo
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Complex karyotype newly defined: the strongest prognostic factor in advanced childhood myelodysplastic syndromeGöhring, Gudrun ; Michalova, Kyra ; Beverloo, H. Berna ; Betts, David ; Harbott, Jochen ; Haas, Oskar A. ; Kerndrup, Gitte ; Sainati, Laura ; Bergstraesser, Eva ; Hasle, Henrik ; Starý, Jan ; Trebo, Monika ; van den Heuvel-Eibrink, Marry M. ; Zecca, Marco ; van Wering, Elisabeth R. ; Fischer, Alexandra ; Noellke, Peter ; Strahm, Brigitte ; Locatelli, Franco ; Niemeyer, Charlotte M. ; Schlegelberger, BrigitteBlood, 2010-11, Vol.116 (19), p.3766-3769 [Periódico revisado por pares]Washington, DC: Elsevier IncTexto completo disponível |