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Lysosomal Storage Diseases. For Better or Worse: Adapting to Defective Lysosomal Glycosphingolipid Breakdown
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Lysosomal Storage Diseases. For Better or Worse: Adapting to Defective Lysosomal Glycosphingolipid Breakdown

Aerts, Johannes M ; Ferraz, Maria J ; Mirzaian, Mina ; Gaspar, Paulo ; Oussoren, Saskia V ; Wisse, Patrick ; Kuo, Chi‐Lin ; Lelieveld, Lindsey T ; Kytidou, Kassiani ; Hazeu, Marc D ; Boer, Daphne EC ; Meijer, Rianne ; Lienden, Martijn JC ; Chao, Daniela HM ; Gabriel, Tanit L ; Aten, Jan ; Overkleeft, Herman S ; Eijk, Marco ; Boot, Rolf G ; Marques, André RA John Wiley & Sons, Ltd

eLS, 2017, p.1-13

Chichester, UK: John Wiley & Sons, Ltd

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