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Material Type: Artigo
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Targeted gene correction of α1-antitrypsin deficiency in induced pluripotent stem cellsYUSA, Kosuke ; TAMIR RASHID, S ; DARCHE, Sylvie ; ALEXANDER, Graeme ; MARCINIAK, Stefan J ; FUSAKI, Noemi ; HASEGAWA, Mamoru ; HOLMES, Michael C ; DI SANTO, James P ; LOMAS, David A ; BRADLEY, Allan ; VALLIER, Ludovic ; STRICK-MARCHAND, Helene ; VARELA, Ignacio ; LIU, Pei-Qi ; PASCHON, David E ; MIRANDA, Elena ; ORDONEZ, Adriana ; HANNAN, Nicholas R. F ; ROUHANI, Foad JNature (London), 2011-10, Vol.478 (7369), p.391-394 [Periódico revisado por pares]London: Nature Publishing GroupTexto completo disponível |
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Material Type: Artigo
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Mesenchymal stem/stromal cells as a pharmacological and therapeutic approach to accelerate angiogenesisBRONCKAERS, Annelies ; HILKENS, Petra ; MARTENS, Wendy ; GERVOIS, Pascal ; RATAJCZAK, Jessica ; STRUYS, Tom ; LAMBRICHTS, IvoPharmacology & therapeutics (Oxford), 2014-08, Vol.143 (2), p.181-196 [Periódico revisado por pares]Oxford: ElsevierTexto completo disponível |
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Material Type: Artigo
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Recognition of Glioma Stem Cells by Genetically Modified T Cells Targeting EGFRvIII and Development of Adoptive Cell Therapy for GliomaMORGAN, Richard A ; JOHNSON, Laura A ; WEI ZHANG ; FINE, Howard A ; ROSENBERG, Steven A ; DAVIS, Jeremy L ; ZHILI ZHENG ; WOOLARD, Kevin D ; REAP, Elizabeth A ; FELDMAN, Steven A ; CHINNASAMY, Nachimuthu ; KUAN, Chien-Tsun ; HUA SONGHuman gene therapy, 2012-10, Vol.23 (10), p.1043-1053 [Periódico revisado por pares]Larchmont, NY: LiebertTexto completo disponível |
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Material Type: Artigo
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Long-Term Evaluation of a Phase 1 Study of AADC Gene Therapy for Parkinson's DiseaseMITTERMEYER, Gabriele ; CHRISTINE, Chadwick W ; ROSENBLUTH, Kathryn H ; BAKER, Suzanne L ; STARR, Philip ; LARSON, Paul ; KAPLAN, Paul L ; FORSAYETH, John ; AMINOFF, Michael J ; BANKIEWICZ, Krystof SHuman gene therapy, 2012-04, Vol.23 (4), p.377-381 [Periódico revisado por pares]Larchmont, NY: LiebertTexto completo disponível |
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Material Type: Artigo
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Prevalence of Serum IgG and Neutralizing Factors Against Adeno-Associated Virus (AAV) Types 1, 2, 5, 6, 8, and 9 in the Healthy Population: Implications for Gene Therapy Using AAV VectorsBOUTIN, Sylvie ; MONTEILHET, Virginie ; VERON, Philippe ; LEBORGNE, Christian ; BENVENISTE, Olivier ; MONTUS, Marie Françoise ; MASURIER, CaroleHuman gene therapy, 2010-06, Vol.21 (6), p.704-712 [Periódico revisado por pares]Larchmont, NY: LiebertTexto completo disponível |
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Material Type: Artigo
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Progress and prospects: immune responses to viral vectorsNAYAK, S ; HERZOG, R. WGene therapy, 2010-03, Vol.17 (3), p.295-304 [Periódico revisado por pares]London: Nature Publishing GroupTexto completo disponível |
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Material Type: Artigo
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Treatment of Leber Congenital Amaurosis Due to RPE65 Mutations by Ocular Subretinal Injection of Adeno-Associated Virus Gene Vector : Short-Term Results of a Phase I TrialHAUSWIRTH, William W ; ALEMAN, Tomas S ; JACOBSON, Samuel G ; KAUSHAL, Shalesh ; CIDECIYAN, Artur V ; SCHWARTZ, Sharon B ; LILI WANG ; CONLON, Thomas J ; BOYE, Sanford L ; FLOTTE, Terence R ; BYRNE, Barry JHuman gene therapy, 2008-10, Vol.19 (10), p.979-990 [Periódico revisado por pares]Larchmont, NY: LiebertTexto completo disponível |
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8 |
Material Type: Artigo
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Optimizing Promoters for Recombinant Adeno-Associated Virus-Mediated Gene Expression in the Peripheral and Central Nervous System Using Self-Complementary VectorsGRAY, Steven J ; FOTI, Stacey B ; SCHWARTZ, Joel W ; BACHABOINA, Lavanya ; TAYLOR-BLAKE, Bonnie ; COLEMAN, Jennifer ; EHLERS, Michael D ; ZYLKA, Mark J ; MCCOWN, Thomas J ; SAMULSKI, R. JudeHuman gene therapy, 2011-09, Vol.22 (9), p.1143-1153 [Periódico revisado por pares]Larchmont, NY: LiebertTexto completo disponível |
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9 |
Material Type: Artigo
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Quantitative Sizing of Nano/Microparticles with a Tunable Elastomeric Pore SensorVogel, Robert ; Willmott, Geoff ; Kozak, Darby ; Roberts, G. Seth ; Anderson, Will ; Groenewegen, Linda ; Glossop, Ben ; Barnett, Anne ; Turner, Ali ; Trau, MattAnalytical chemistry (Washington), 2011-05, Vol.83 (9), p.3499-3506 [Periódico revisado por pares]Washington, DC: American Chemical SocietyTexto completo disponível |
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10 |
Material Type: Artigo
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Embryonic stem cell trials for macular degeneration: a preliminary reportSchwartz, Steven D, Prof ; Hubschman, Jean-Pierre, MD ; Heilwell, Gad, MD ; Franco-Cardenas, Valentina, MD ; Pan, Carolyn K, MD ; Ostrick, Rosaleen M, MPH ; Mickunas, Edmund, MS ; Gay, Roger, PhD ; Klimanskaya, Irina, PhD ; Lanza, Robert, DrThe Lancet (British edition), 2012-02, Vol.379 (9817), p.713-720 [Periódico revisado por pares]Kidlington: Elsevier LtdTexto completo disponível |