Result Number | Material Type | Add to My Shelf Action | Record Details and Options |
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1 |
Material Type: Livro
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Nonviral Vectors for Gene TherapyMien-Chie Huang, Leaf Wagner, Ernst Hung Leaf Huang; Mien-chie Hung; Ernst Wagner Ernst Wagner Leaf HuangBurlington Academic Press 1999Acesso online. A biblioteca também possui exemplares impressos. |
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2 |
Material Type: Livro
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Adeno-Associated Viral Vectors for Gene TherapyKenneth I Berns; Terence Robin FlotteElsevier 2005Acesso online. A biblioteca também possui exemplares impressos. |
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3 |
Material Type: Livro
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Adenoviral Vectors for Gene TherapyDavid T. Douglas, Joanne T. Douglas, Joanne T Curiel David Curiel; Joanne T Douglas; David T. Curiel; Joanne T. DouglasAcademic Press 2002Acesso online. A biblioteca também possui exemplares impressos. |
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4 |
Material Type: Livro
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Gene therapy protocolsJoseph M Le DouxTotowa, NJ Humana Press c2008-Localização: FZEA - Fac. Zoot. Eng. de Alimentos (QH581.2 L433g 2008 v.2 )(Acessar) |
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5 |
Material Type: Artigo
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Long-term safety and efficacy of lentiviral hematopoietic stem/progenitor cell gene therapy for Wiskott-Aldrich syndromeMagnani, A ; Semeraro, M ; Adam, F ; Booth, C ; Dupré, L ; Morris, E C ; Gabrion, A ; Roudaut, C ; Borgel, D ; Toubert, A ; Clave, E ; Abdo, C ; Gorochov, G ; Petermann, R ; Guiot, M ; Miyara, M ; Moshous, D ; Magrin, E ; Denis, A ; Suarez, F ; Lagresle, C ; Roche, A M ; Everett, J ; Trinquand, A ; Guisset, M ; Bayford, J Xu ; Hacein-Bey-Abina, S ; Kauskot, A ; Elfeky, R ; Rivat, C ; Abbas, S ; Gaspar, H B ; Macintyre, E ; Picard, C ; Bushman, F D ; Galy, A ; Fischer, A ; Six, E ; Thrasher, A J ; Cavazzana, MNature Medicine, 2022-01, Vol.28 (1), p.71-80 [Periódico revisado por pares]United States: Nature Publishing GroupTexto completo disponível |
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6 |
Material Type: Artigo
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Engineering adeno-associated viruses for clinical gene therapyKotterman, Melissa A ; Schaffer, David VNature reviews. Genetics, 2014-07, Vol.15 (7), p.445-451 [Periódico revisado por pares]England: Nature Publishing GroupTexto completo disponível |
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7 |
Material Type: Artigo
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Treatment of a metabolic liver disease by in vivo genome base editing in adult miceVilliger, Lukas ; Grisch-Chan, Hiu Man ; Lindsay, Helen ; Ringnalda, Femke ; Pogliano, Chiara B ; Allegri, Gabriella ; Fingerhut, Ralph ; Häberle, Johannes ; Matos, Joao ; Robinson, Mark D ; Thöny, Beat ; Schwank, GeraldNature medicine, 2018-10, Vol.24 (10), p.1519-1525 [Periódico revisado por pares]United States: Nature Publishing GroupTexto completo disponível |
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8 |
Material Type: Artigo
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Therapeutic in vivo gene transfer for genetic disease using AAV: progress and challengesHigh, Katherine A ; Mingozzi, FedericoNature reviews. Genetics, 2011-05, Vol.12 (5), p.341-355 [Periódico revisado por pares]England: Nature Publishing GroupTexto completo disponível |
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9 |
Material Type: Artigo
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Partial recovery of visual function in a blind patient after optogenetic therapySahel, José-Alain ; Boulanger-Scemama, Elise ; Pagot, Chloé ; Arleo, Angelo ; Galluppi, Francesco ; Martel, Joseph N ; Esposti, Simona Degli ; Delaux, Alexandre ; de Saint Aubert, Jean-Baptiste ; de Montleau, Caroline ; Gutman, Emmanuel ; Audo, Isabelle ; Duebel, Jens ; Picaud, Serge ; Dalkara, Deniz ; Blouin, Laure ; Taiel, Magali ; Roska, BotondNature Medicine, 2021-07, Vol.27 (7), p.1223-1229 [Periódico revisado por pares]United States: Nature Publishing GroupTexto completo disponível |
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10 |
Material Type: Artigo
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Assessment of Systemic Delivery of rAAVrh74.MHCK7.micro-dystrophin in Children With Duchenne Muscular Dystrophy: A Nonrandomized Controlled TrialMendell, Jerry R ; Sahenk, Zarife ; Lehman, Kelly ; Nease, Carrie ; Lowes, Linda P ; Miller, Natalie F ; Iammarino, Megan A ; Alfano, Lindsay N ; Nicholl, Amanda ; Al-Zaidy, Samiah ; Lewis, Sarah ; Church, Kathleen ; Shell, Richard ; Cripe, Linda H ; Potter, Rachael A ; Griffin, Danielle A ; Pozsgai, Eric ; Dugar, Ashish ; Hogan, Mark ; Rodino-Klapac, Louise RJAMA neurology, 2020-09, Vol.77 (9), p.1122-1131 [Periódico revisado por pares]United States: American Medical AssociationTexto completo disponível |