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Refinado por: assunto: Hematology remover
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1
Efficacy and safety of azacitidine in pediatric patients with newly diagnosed advanced myelodysplastic syndromes before hematopoietic stem cell transplantation in the AZA‐JMML‐001 trial
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Efficacy and safety of azacitidine in pediatric patients with newly diagnosed advanced myelodysplastic syndromes before hematopoietic stem cell transplantation in the AZA‐JMML‐001 trial

Locatelli, Franco ; Strålin, Karin Belander ; Schmid, Irene ; Sevilla, Julián ; Smith, Owen P. ; den Heuvel‐Eibrink, Marry M. ; Zecca, Marco ; Zwaan, Christian M. ; Gaudy, Allison ; Patturajan, Meera ; Poon, Jennifer ; Simcock, Mathew ; Niemeyer, Charlotte M.

Pediatric blood & cancer, 2024-05, Vol.71 (5), p.e30931-n/a [Periódico revisado por pares]

United States: Wiley Subscription Services, Inc

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2
International Consensus Classification of Myeloid Neoplasms and Acute Leukemias: integrating morphologic, clinical, and genomic data
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Artigo
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International Consensus Classification of Myeloid Neoplasms and Acute Leukemias: integrating morphologic, clinical, and genomic data

Arber, Daniel A ; Orazi, Attilio ; Hasserjian, Robert P ; Borowitz, Michael J ; Calvo, Katherine R ; Kvasnicka, Hans-Michael ; Wang, Sa A ; Bagg, Adam ; Barbui, Tiziano ; Branford, Susan ; Bueso-Ramos, Carlos E ; Cortes, Jorge E ; Dal Cin, Paola ; DiNardo, Courtney D ; Dombret, Hervé ; Duncavage, Eric J ; Ebert, Benjamin L ; Estey, Elihu H ; Facchetti, Fabio ; Foucar, Kathryn ; Gangat, Naseema ; Gianelli, Umberto ; Godley, Lucy A ; Gökbuget, Nicola ; Gotlib, Jason ; Hellström-Lindberg, Eva ; Hobbs, Gabriela S ; Hoffman, Ronald ; Jabbour, Elias J ; Kiladjian, Jean-Jacques ; Larson, Richard A ; Le Beau, Michelle M ; Loh, Mignon L-C ; Löwenberg, Bob ; Macintyre, Elizabeth ; Malcovati, Luca ; Mullighan, Charles G ; Niemeyer, Charlotte ; Odenike, Olatoyosi M ; Ogawa, Seishi ; Orfao, Alberto ; Papaemmanuil, Elli ; Passamonti, Francesco ; Porkka, Kimmo ; Pui, Ching-Hon ; Radich, Jerald P ; Reiter, Andreas ; Rozman, Maria ; Rudelius, Martina ; Savona, Michael R ; Schiffer, Charles A ; Schmitt-Graeff, Annette ; Shimamura, Akiko ; Sierra, Jorge ; Stock, Wendy A ; Stone, Richard M ; Tallman, Martin S ; Thiele, Jürgen ; Tien, Hwei-Fang ; Tzankov, Alexandar ; Vannucchi, Alessandro M ; Vyas, Paresh ; Wei, Andrew H ; Weinberg, Olga K ; Wierzbowska, Agnieszka ; Cazzola, Mario ; Döhner, Hartmut ; Tefferi, Ayalew

Blood, 2022-09, Vol.140 (11), p.1200-1228 [Periódico revisado por pares]

United States: American Society of Hematology

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3
Risk-adjusted therapy of acute lymphoblastic leukemia can decrease treatment burden and improve survival: treatment results of 2169 unselected pediatric and adolescent patients enrolled in the trial ALL-BFM 95
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Risk-adjusted therapy of acute lymphoblastic leukemia can decrease treatment burden and improve survival: treatment results of 2169 unselected pediatric and adolescent patients enrolled in the trial ALL-BFM 95

Möricke, Anja ; Reiter, Alfred ; Zimmermann, Martin ; Gadner, Helmut ; Stanulla, Martin ; Dördelmann, Michael ; Löning, Lutz ; Beier, Rita ; Ludwig, Wolf-Dieter ; Ratei, Richard ; Harbott, Jochen ; Boos, Joachim ; Mann, Georg ; Niggli, Felix ; Feldges, Andreas ; Henze, Günter ; Welte, Karl ; Beck, Jörn-Dirk ; Klingebiel, Thomas ; Niemeyer, Charlotte ; Zintl, Felix ; Bode, Udo ; Urban, Christian ; Wehinger, Helmut ; Niethammer, Dietrich ; Riehm, Hansjörg ; Schrappe, Martin

Blood, 2008-05, Vol.111 (9), p.4477-4489 [Periódico revisado por pares]

Washington, DC: Elsevier Inc

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4
Loss of B cells and their precursors is the most constant feature of GATA-2 deficiency in childhood myelodysplastic syndrome
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Artigo
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Loss of B cells and their precursors is the most constant feature of GATA-2 deficiency in childhood myelodysplastic syndrome

Nováková, Michaela ; Žaliová, Markéta ; Suková, Martina ; Wlodarski, Marcin ; Janda, Aleš ; Froňková, Eva ; Campr, Vít ; Lejhancová, Kateřina ; Zapletal, Ondřej ; Pospíšilová, Dagmar ; Černá, Zdeňka ; Kuhn, Tomáš ; Švec, Peter ; Pelková, Vendula ; Zemanová, Zuzana ; Kerndrup, Gitte ; van den Heuvel-Eibrink, Marry ; van der Velden, Vincent ; Niemeyer, Charlotte ; Kalina, Tomáš ; Trka, Jan ; Starý, Jan ; Hrušák, Ondřej ; Mejstříková, Ester

Haematologica (Roma), 2016-06, Vol.101 (6), p.707-716 [Periódico revisado por pares]

Italy: Ferrata Storti Foundation

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5
Criteria for evaluating response and outcome in clinical trials for children with juvenile myelomonocytic leukemia
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Artigo
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Criteria for evaluating response and outcome in clinical trials for children with juvenile myelomonocytic leukemia

Niemeyer, Charlotte M ; Loh, Mignon L ; Cseh, Annamaria ; Cooper, Todd ; Dvorak, Christopher C ; Chan, Rebecca ; Xicoy, Blanca ; Germing, Ulrich ; Kojima, Seiji ; Manabe, Atsushi ; Dworzak, Michael ; De Moerloose, Barbara ; Starý, Jan ; Smith, Owen P ; Masetti, Riccardo ; Catala, Albert ; Bergstraesser, Eva ; Ussowicz, Marek ; Fabri, Oskana ; Baruchel, André ; Cavé, Hélène ; Zwaan, Michel ; Locatelli, Franco ; Hasle, Henrik ; van den Heuvel-Eibrink, Marry M ; Flotho, Christian ; Yoshimi, Ayami

Haematologica (Roma), 2015-01, Vol.100 (1), p.17-22 [Periódico revisado por pares]

Italy: Ferrata Storti Foundation

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6
NDEL1-PDGFRB fusion gene in a myeloid malignancy with eosinophilia associated with resistance to tyrosine kinase inhibitors
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Artigo
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NDEL1-PDGFRB fusion gene in a myeloid malignancy with eosinophilia associated with resistance to tyrosine kinase inhibitors

Byrgazov, K ; Kastner, R ; Gorna, M ; Hoermann, G ; Koenig, M ; Lucini, C B ; Ulreich, R ; Benesch, M ; Strenger, V ; Lackner, H ; Schwinger, W ; Sovinz, P ; Haas, O A ; van den Heuvel-Eibrink, M ; Niemeyer, C M ; Hantschel, O ; Valent, P ; Superti-Furga, G ; Urban, C ; Dworzak, M N ; Lion, T

Leukemia, 2017-01, Vol.31 (1), p.237-240 [Periódico revisado por pares]

England: Nature Publishing Group

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7
Comparison of horse and rabbit antithymocyte globulin in immunosuppressive therapy for refractory cytopenia of childhood
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Artigo
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Comparison of horse and rabbit antithymocyte globulin in immunosuppressive therapy for refractory cytopenia of childhood

Yoshimi, Ayami ; van den Heuvel-Eibrink, Marry M ; Baumann, Irith ; Schwarz, Stephan ; Simonitsch-Klupp, Ingrid ; de Paepe, Pascale ; Campr, Vit ; Kerndrup, Gitte Birk ; O'Sullivan, Maureen ; Devito, Rita ; Leguit, Roos ; Hernandez, Miguel ; Dworzak, Michael ; de Moerloose, Barbara ; Stary, Jan ; Hasle, Henrik ; Smith, Owen P ; Zecca, Marco ; Catala, Albert ; Schmugge, Markus ; Locatelli, Franco ; Führer, Monika ; Fischer, Alexandra ; Guderle, Anne ; Nöllke, Peter ; Strahm, Brigitte ; Niemeyer, Charlotte M

Haematologica (Roma), 2014-04, Vol.99 (4), p.656-663 [Periódico revisado por pares]

Italy: Ferrata Storti Foundation

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8
The level of residual disease based on mutant NPM1 is an independent prognostic factor for relapse and survival in AML
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Artigo
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The level of residual disease based on mutant NPM1 is an independent prognostic factor for relapse and survival in AML

Shayegi, Nona ; Kramer, Michael ; Bornhäuser, Martin ; Schaich, Markus ; Schetelig, Johannes ; Platzbecker, Uwe ; Röllig, Christoph ; Heiderich, Caroline ; Landt, Olfert ; Ehninger, Gerhard ; Thiede, Christian

Blood, 2013-07, Vol.122 (1), p.83-92 [Periódico revisado por pares]

United States: Elsevier Inc

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9
Chronic myelomonocytic leukemia in childhood : A retrospective analysis of 110 cases
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Artigo
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Chronic myelomonocytic leukemia in childhood : A retrospective analysis of 110 cases

NIEMEYER, C. M ; ARICO, M ; LOCATELLI, F ; MANN, G ; STOLLMANN-GIBBELS, B ; VAN'T VEER-KORTHOF, E. T ; VAN WERING, E ; ZIMMERMANN, M ; BASSO, G ; BIONDI, A ; RAJNOLDI, A. C ; CREUTZIG, U ; HAAS, O ; HARBOTT, J ; HASLE, H ; KERNDRUP, G

Blood, 1997-05, Vol.89 (10), p.3534-3543 [Periódico revisado por pares]

Washington, DC: The Americain Society of Hematology

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10
Myelodysplastic syndrome, juvenile myelomonocytic leukemia, and acute myeloid leukemia associated with complete or partial monosomy 7
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Artigo
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Myelodysplastic syndrome, juvenile myelomonocytic leukemia, and acute myeloid leukemia associated with complete or partial monosomy 7

HASLE, H ; ARICO, M ; KARDOS, G ; KERNDRUP, G ; MANN, G ; NIEMEYER, C ; PTOSZKOVA, H ; RITTER, J ; SLATER, R ; STARY, J ; STOLLMANN-GIBBELS, B ; TESTI, A ; BASSO, G ; VAN WERING, E ; ZIMMERMANN, M ; BIONDI, A ; RAJNOLDI, A. C ; CREUTZIG, U ; FENU, S ; FONATSCH, C ; HAAS, O ; HARBOTT, J

Leukemia, 1999-03, Vol.13 (3), p.376-385 [Periódico revisado por pares]

London: Nature Publishing

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