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Current Strategies for Increasing Knock-In Efficiency in CRISPR/Cas9-Based ApproachesLeal, Andrés Felipe ; Herreno-Pachón, Angelica María ; Benincore-Flórez, Eliana ; Karunathilaka, Amali ; Tomatsu, ShunjiInternational journal of molecular sciences, 2024-02, Vol.25 (5), p.2456 [Periódico revisado por pares]Switzerland: MDPI AGTexto completo disponível |
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GM2 Gangliosidoses: Clinical Features, Pathophysiological Aspects, and Current TherapiesLeal, Andrés Felipe ; Benincore-Flórez, Eliana ; Solano-Galarza, Daniela ; Garzón Jaramillo, Rafael Guillermo ; Echeverri-Peña, Olga Yaneth ; Suarez, Diego A ; Alméciga-Díaz, Carlos Javier ; Espejo-Mojica, Angela JohanaInternational journal of molecular sciences, 2020-08, Vol.21 (17), p.6213 [Periódico revisado por pares]Switzerland: MDPI AGTexto completo disponível |
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Material Type: Artigo
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Mucopolysaccharidosis IVA: Current Disease Models and DrawbacksLeal, Andrés Felipe ; Alméciga-Díaz, Carlos Javier ; Tomatsu, ShunjiInternational journal of molecular sciences, 2023-11, Vol.24 (22), p.16148 [Periódico revisado por pares]Switzerland: MDPI AGTexto completo disponível |
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Material Type: Artigo
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Regulation of Molecular Targets in Osteosarcoma TreatmentCelik, Betul ; Cicek, Kader ; Leal, Andrés Felipe ; Tomatsu, ShunjiInternational journal of molecular sciences, 2022-10, Vol.23 (20), p.12583 [Periódico revisado por pares]Basel: MDPI AGTexto completo disponível |
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Material Type: Artigo
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CRISPR/nCas9-Based Genome Editing on GM2 Gangliosidoses Fibroblasts via Non-Viral VectorsLeal, Andrés Felipe ; Cifuentes, Javier ; Quezada, Valentina ; Benincore-Flórez, Eliana ; Cruz, Juan Carlos ; Reyes, Luis Humberto ; Espejo-Mojica, Angela Johana ; Alméciga-Díaz, Carlos JavierInternational journal of molecular sciences, 2022-09, Vol.23 (18), p.10672 [Periódico revisado por pares]Basel: MDPI AGTexto completo disponível |
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Material Type: Artigo
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Small molecules present in the cerebrospinal fluid metabolome influence superoxide dismutase 1 aggregationCristóvão, Joana S ; Leal, Sónia S ; Cardoso, Isabel ; Gomes, Cláudio MInternational journal of molecular sciences, 2013-09, Vol.14 (9), p.19128-19145 [Periódico revisado por pares]Switzerland: MDPI AGTexto completo disponível |
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Material Type: Artigo
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Rare Variants in Genes of the Cholesterol Pathway Are Present in 60% of Patients with Acute Myocardial InfarctionPan-Lizcano, Ricardo ; Mariñas-Pardo, Luis ; Núñez, Lucía ; Rebollal-Leal, Fernando ; López-Vázquez, Domingo ; Pereira, Ana ; Molina-Nieto, Aranzazu ; Calviño, Ramón ; Vázquez-Rodríguez, Jose Manuel ; Hermida-Prieto, ManuelInternational journal of molecular sciences, 2022-12, Vol.23 (24), p.16127 [Periódico revisado por pares]Switzerland: MDPI AGTexto completo disponível |
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Material Type: Artigo
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SARS-CoV-2 Spatiotemporal Genomic and Molecular Analysis of the First Wave of the COVID-19 Pandemic in Macaé, the Brazilian Capital of Oilda-Costa-Rodrigues, Bruno ; Cheohen, Caio ; Sciammarella, Felipe ; Pierre-Bonetti-Pozzobon, Allan ; Ribeiro, Lupis ; Nepomuceno-Silva, José Luciano ; Medeiros, Marcio ; Mury, Flávia ; Monteiro-de-Barros, Cintia ; Lazoski, Cristiano ; Leal-da-Silva, Manuela ; Tanuri, Amilcar ; Nunes-da-Fonseca, RodrigoInternational journal of molecular sciences, 2022-10, Vol.23 (19), p.11497 [Periódico revisado por pares]Basel: MDPI AGTexto completo disponível |
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Material Type: Artigo
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ELF3 Is a Target That Promotes Therapeutic Efficiency in EGFR Tyrosine Kinase Inhibitor-Resistant Non-Small Cell Lung Cancer Cells via Inhibiting PKCίLee, Jeon-Soo ; Choi, Young Eun ; Kim, Sunshin ; Han, Ji-Youn ; Goh, Sung-HoInternational journal of molecular sciences, 2021-11, Vol.22 (22), p.12287 [Periódico revisado por pares]Switzerland: MDPI AGTexto completo disponível |
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Material Type: Artigo
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In the Eyes of the Beholder-New Mertk Knockout Mouse and Re-Evaluation of Phagocytosis versus Anti-Inflammatory Functions of MERTKGhosh, Sourav ; Finnemann, Silvia C ; Vollrath, Douglas ; Rothlin, Carla VInternational journal of molecular sciences, 2024-05, Vol.25 (10), p.5299 [Periódico revisado por pares]Switzerland: MDPI AGTexto completo disponível |