BMN 250, a fusion of lysosomal alpha-N-acetylglucosaminidase with IGF2, exhibits different patterns of cellular uptake into critical cell types of Sanfilippo syndrome B disease pathogenesis

Yogalingam, Gouri ; Luu, Amanda R ; Prill, Heather ; Lo, Melanie J ; Yip, Bryan ; Holtzinger, John ; Christianson, Terri ; Aoyagi-Scharber, Mika ; Lawrence, Roger ; Crawford, Brett E ; LeBowitz, Jonathan H Dardis, Andrea

United States: Public Library of Science

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Delivery of an enzyme-IGFII fusion protein to the mouse brain is therapeutic for mucopolysaccharidosis type IIIB

Kan, Shih-hsin ; Aoyagi-Scharber, Mika ; Le, Steven Q. ; Vincelette, Jon ; Ohmi, Kazuhiro ; Bullens, Sherry ; Wendt, Daniel J. ; Christiansen, Terri M. ; Tiger, Pascale M. N. ; Brown, Julian R. ; Lawrence, Roger ; Yip, Bryan K. ; Holtzinger, John ; Bagri, Anil ; Crippen-Harmon, Danielle ; Vondrak, Kristen N. ; Chen, Zhi ; Hague, Chuck M. ; Woloszynek, Josh C. ; Cheung, Diana S. ; Webster, Katherine A. ; Adintori, Evan G. ; Lo, Melanie J. ; Wong, Wesley ; Fitzpatrick, Paul A. ; LeBowitz, Jonathan H. ; Crawford, Brett E. ; Bunting, Stuart ; Dickson, Patricia I. ; Neufeld, Elizabeth F.

United States: National Academy of Sciences

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Clearance of Heparan Sulfate and Attenuation of CNS Pathology by Intracerebroventricular BMN 250 in Sanfilippo Type B Mice

Aoyagi-Scharber, Mika ; Crippen-Harmon, Danielle ; Lawrence, Roger ; Vincelette, Jon ; Yogalingam, Gouri ; Prill, Heather ; Yip, Bryan K ; Baridon, Brian ; Vitelli, Catherine ; Lee, Amanda ; Gorostiza, Olivia ; Adintori, Evan G ; Minto, Wesley C ; Van Vleet, Jeremy L ; Yates, Bridget ; Rigney, Sara ; Christianson, Terri M ; Tiger, Pascale M N ; Lo, Melanie J ; Holtzinger, John ; Fitzpatrick, Paul A ; LeBowitz, Jonathan H ; Bullens, Sherry ; Crawford, Brett E ; Bunting, Stuart

United States: Elsevier Limited

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Differential Uptake of NAGLU-IGF2 and Unmodified NAGLU in Cellular Models of Sanfilippo Syndrome Type B

Prill, Heather ; Luu, Amanda ; Yip, Bryan ; Holtzinger, John ; Lo, Melanie J. ; Christianson, Terri M. ; Yogalingam, Gouri ; Aoyagi-Scharber, Mika ; LeBowitz, Jonathan H. ; Crawford, Brett E. ; Lawrence, Roger

United States: Elsevier Inc

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Regulation of a vascular plexus by gata4 is mediated in zebrafish through the chemokine sdf1a

Torregroza, Ingrid ; Holtzinger, Audrey ; Mendelson, Karen ; Liu, Ting-Chun ; Hla, Timothy ; Evans, Todd Henrique, Domingos

United States: Public Library of Science

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Author index

London: BMJ Publishing Group LTD

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Selenoprotein H is an essential regulator of redox homeostasis that cooperates with p53 in development and tumorigenesis

Cox, Andrew G. ; Tsomides, Allison ; Kim, Andrew J. ; Saunders, Diane ; Hwang, Katie L. ; Evason, Kimberley J. ; Heidel, Jerry ; Brown, Kristin K. ; Yuan, Min ; Lien, Evan C. ; Lee, Byung Cheon ; Nissim, Sahar ; Dickinson, Bryan ; Chhangawala, Sagar ; Chang, Christopher J. ; Asara, John M. ; Houvras, Yariv ; Gladyshev, Vadim N. ; Goessling, Wolfram

United States: National Academy of Sciences

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Sustained levels of FGF2 maintain undifferentiated stem cell cultures with biweekly feeding

Lotz, Steven ; Goderie, Susan ; Tokas, Nicolas ; Hirsch, Sarah E ; Ahmad, Faizzan ; Corneo, Barbara ; Le, Sheila ; Banerjee, Akhilesh ; Kane, Ravi S ; Stern, Jeffrey H ; Temple, Sally ; Fasano, Christopher A Pereira, Lygia V.

United States: Public Library of Science

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Unlimited in vitro expansion of adult bi-potent pancreas progenitors through the Lgr5/R-spondin axis

Huch, Meritxell ; Bonfanti, Paola ; Boj, Sylvia F ; Sato, Toshiro ; Loomans, Cindy J M ; van de Wetering, Marc ; Sojoodi, Mozhdeh ; Li, Vivian S W ; Schuijers, Jurian ; Gracanin, Ana ; Ringnalda, Femke ; Begthel, Harry ; Hamer, Karien ; Mulder, Joyce ; van Es, Johan H ; de Koning, Eelco ; Vries, Robert G J ; Heimberg, Harry ; Clevers, Hans

Chichester, UK: John Wiley & Sons, Ltd

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Intracerebroventricular enzyme replacement therapy with β-galactosidase reverses brain pathologies due to GM1 gangliosidosis in mice

Chen, Joseph C. ; Luu, Amanda R. ; Wise, Nathan ; Angelis, Rolando De ; Agrawal, Vishal ; Mangini, Linley ; Vincelette, Jon ; Handyside, Britta ; Sterling, Harry ; Lo, Melanie J. ; Wong, Hio ; Galicia, Nicole ; Pacheco, Glenn ; Van Vleet, Jeremy ; Giaramita, Alexander ; Fong, Sylvia ; Roy, Sushmita M. ; Hague, Chuck ; Lawrence, Roger ; Bullens, Sherry ; Christianson, Terri M. ; d'Azzo, Alessandra ; Crawford, Brett E. ; Bunting, Stuart ; LeBowitz, Jonathan H. ; Yogalingam, Gouri

United States: Elsevier Inc

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