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Regulated hAAT Expression from a Novel rAAV Vector and Its Application in the Prevention of Type 1 Diabetes

Ma, Hongxia ; Lu, Yuanqing ; Lowe, Keith ; van der Meijden-Erkelens, Lonneke ; Wasserfall, Clive ; Atkinson, Mark A ; Song, Sihong

Journal of clinical medicine, 2019-08, Vol.8 (9), p.1321 [Periódico revisado por pares]

Switzerland: MDPI

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