A genome-editing strategy to treat β-hemoglobinopathies that recapitulates a mutation associated with a benign genetic condition

Traxler, Elizabeth A ; Yao, Yu ; Wang, Yong-Dong ; Woodard, Kaitly J ; Kurita, Ryo ; Nakamura, Yukio ; Hughes, Jim R ; Hardison, Ross C ; Blobel, Gerd A ; Li, Chunliang ; Weiss, Mitchell J

Nature medicine, 2016-09, Vol.22 (9), p.987-990 [Periódico revisado por pares]

United States

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