Efficacy and safety of givosiran for acute hepatic porphyria: 24‐month interim analysis of the randomized phase 3 ENVISION study

Ventura, Paolo ; Bonkovsky, Herbert L. ; Gouya, Laurent ; Aguilera‐Peiró, Paula ; Montgomery Bissell, D. ; Stein, Penelope E. ; Balwani, Manisha ; Anderson, D. Karl E. ; Parker, Charles ; Kuter, David J. ; Monroy, Susana ; Oh, Jeeyoung ; Ritchie, Bruce ; Ko, John J. ; Hua, Zhaowei ; Sweetser, Marianne T. ; Sardh, Eliane

Liver international, 2022-01, Vol.42 (1), p.161-172 [Periódico revisado por pares]

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