Evidence of Treatment Benefits in Patients with Mucopolysaccharidosis Type I-Hurler in Long-term Follow-up Using a New Magnetic Resonance Imaging Scoring System

Pontesilli, Silvia ; Baldoli, Cristina ; Rosa, Pasquale Anthony Della ; Cattoni, Alessandro ; Bernardo, Maria Ester ; Meregalli, Pamela ; Gasperini, Serena ; Motta, Serena ; Fumagalli, Francesca ; Tucci, Francesca ; Baciga, Federica ; Consiglieri, Giulia ; Canonico, Francesco ; De Lorenzo, Paola ; Chiapparini, Luisa ; Gentner, Bernhard ; Aiuti, Alessandro ; Biondi, Andrea ; Rovelli, Attilio ; Parini, Rossella

The Journal of pediatrics, 2022-01, Vol.240, p.297-301.e5 [Periódico revisado por pares]

United States: Elsevier Inc

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