Engineering Multiple U7snRNA Constructs to Induce Single and Multiexon-skipping for Duchenne Muscular Dystrophy
Goyenvalle, Aurélie ; Wright, Jordan ; Babbs, Arran ; Wilkins, Vivienne ; Garcia, Luis ; Davies, Kay E
Molecular therapy, 2012-06, Vol.20 (6), p.1212-1221 [Periódico revisado por pares]United States: Elsevier Inc
Texto completo disponível