Engineering Multiple U7snRNA Constructs to Induce Single and Multiexon-skipping for Duchenne Muscular Dystrophy

Goyenvalle, Aurélie ; Wright, Jordan ; Babbs, Arran ; Wilkins, Vivienne ; Garcia, Luis ; Davies, Kay E

Molecular therapy, 2012-06, Vol.20 (6), p.1212-1221 [Periódico revisado por pares]

United States: Elsevier Inc

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