Follistatin Gene Therapy for Sporadic Inclusion Body Myositis Improves Functional Outcomes
Mendell, Jerry R. ; Sahenk, Zarife ; Al-Zaidy, Samiah ; Rodino-Klapac, Louise R. ; Lowes, Linda P. ; Alfano, Lindsay N. ; Berry, Katherine ; Miller, Natalie ; Yalvac, Mehmet ; Dvorchik, Igor ; Moore-Clingenpeel, Melissa ; Flanigan, Kevin M. ; Church, Kathleen ; Shontz, Kim ; Curry, Choumpree ; Lewis, Sarah ; McColly, Markus ; Hogan, Mark J. ; Kaspar, Brian K.
Molecular therapy, 2017-04, Vol.25 (4), p.870-879 [Periódico revisado por pares]United States: Elsevier Inc
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