Oligonucleotide therapy mitigates disease in spinocerebellar ataxia type 3 mice
McLoughlin, Hayley S. ; Moore, Lauren R. ; Chopra, Ravi ; Komlo, Robert ; McKenzie, Megan ; Blumenstein, Kate G. ; Zhao, Hien ; Kordasiewicz, Holly B. ; Shakkottai, Vikram G. ; Paulson, Henry L.
Annals of neurology, 2018-07, Vol.84 (1), p.64-77 [Periódico revisado por pares]United States: Wiley Subscription Services, Inc
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