Non-immunogenic utrophin gene therapy for the treatment of muscular dystrophy animal models

Song, Yafeng ; Morales, Leon ; Malik, Alock S ; Mead, Andrew F ; Greer, Christopher D ; Mitchell, Marilyn A ; Petrov, Mihail T ; Su, Leonard T ; Choi, Margaret E ; Rosenblum, Shira T ; Lu, Xiangping ; VanBelzen, Daniel J ; Krishnankutty, Ranjith K ; Balzer, Frederick J ; Loro, Emanuele ; French, Robert ; Propert, Kathleen J ; Zhou, Shangzhen ; Kozyak, Benjamin W ; Nghiem, Peter P ; Khurana, Tejvir S ; Kornegay, Joe N ; Stedman, Hansell H

Nature medicine, 2019-10, Vol.25 (10), p.1505-1511 [Periódico revisado por pares]

United States: Nature Publishing Group

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