PCR137 Within-Trial Interviews to Contextualize the Patient Experience and Supplement Clinical Outcomes Assessments in a Pivotal Trial of a Newly Described, Fatal and Ultra-Rare Pediatric Disease

Litcher-Kelly, L ; Ozen, A ; Ollis, S ; Feldman H, Baris ; Yaworsky, A ; Medrano, P ; Chongsrisawat, V ; Brackin, T ; Perlee, L ; Walker, M ; Pradeep, S ; Lenardo, MJ ; Harari, O ; Jalbert, JJ

Value in health, 2024-06, Vol.27 (6), p.S321-S321 [Periódico revisado por pares]

Elsevier Inc

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