Gene Augmentation of CHM Using Non-Viral Episomal Vectors in Models of Choroideremia
Toualbi, Lyes ; Toms, Maria ; Almeida, Patrick Vingadas ; Harbottle, Richard ; Moosajee, Mariya
International journal of molecular sciences, 2023-10, Vol.24 (20), p.15225 [Periódico revisado por pares]Switzerland: MDPI AG
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