Enzyme Replacement Therapy in Mucopolysaccharidosis II Patients Under 1 Year of Age

Lampe, Christina ; Atherton, Andrea ; Burton, Barbara K. ; Descartes, Maria ; Giugliani, Roberto ; Horovitz, Dafne D. G. ; Kyosen, Sandra O. ; Magalhães, Tatiana S. P. C. ; Martins, Ana Maria ; Mendelsohn, Nancy J. ; Muenzer, Joseph ; Smith, Laurie D. Peters, Verena ; Gibson, K. Michael ; Zschocke, Johannes ; Brown, Garry ; Morava, Eva

JIMD Reports, Volume 14, 2014, Vol.14, p.99-113 [Periódico revisado por pares]

Berlin, Heidelberg: Springer Berlin Heidelberg

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