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Lentiviral Hematopoietic Stem Cell Gene Therapy in Patients with Wiskott-Aldrich Syndrome

Aiuti, Alessandro ; Biasco, Luca ; Scaramuzza, Samantha ; Ferrua, Francesca ; Cicalese, Maria Pia ; Baricordi, Cristina ; Dionisio, Francesca ; Calabria, Andrea ; Giannelli, Stefania ; Castiello, Maria Carmina ; Bosticardo, Marita ; Evangelio, Costanza ; Assanelli, Andrea ; Casiraghi, Miriam ; Di Nunzio, Sara ; Callegaro, Luciano ; Benati, Claudia ; Rizzardi, Paolo ; Pellin, Danilo ; Di Serio, Clelia ; Schmidt, Manfred ; Von Kalle, Christof ; Gardner, Jason ; Mehta, Nalini ; Neduva, Victor ; Dow, David J. ; Galy, Anne ; Miniero, Roberto ; Finocchi, Andrea ; Metin, Ayse ; Banerjee, Pinaki P. ; Orange, Jordan S. ; Galimberti, Stefania ; Valsecchi, Maria Grazia ; Biffi, Alessandra ; Montini, Eugenio ; Villa, Anna ; Ciceri, Fabio ; Roncarolo, Maria Grazia ; Naldini, Luigi

Science (American Association for the Advancement of Science), 2013-08, Vol.341 (6148), p.865-865 [Periódico revisado por pares]

United States: American Association for the Advancement of Science

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