Impact of ERT and follow-up of 17 patients from the same family with a mild form of MPS II
Bruno de Oliveira Stephan Caio Robledo Quaio; Gustavo Marquezani Spolador; Ana Carolina de Paula; Marco Antonio Curiati; Ana Maria Martins; Gabriela Nunes Leal; Artur Tenorio; Carla Gentile Matas; Chong Ae Kim
Clinics v. 77, article ID 100082, 6p, 2022Brazil 2022
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