Long-term evaluation of AAV-CRISPR genome editing for Duchenne muscular dystrophy

Nelson, Christopher E ; Wu, Yaoying ; Gemberling, Matthew P ; Oliver, Matthew L ; Waller, Matthew A ; Bohning, Joel D ; Robinson-Hamm, Jacqueline N ; Bulaklak, Karen ; Castellanos Rivera, Ruth M ; Collier, Joel H ; Asokan, Aravind ; Gersbach, Charles A

Nature medicine, 2019-03, Vol.25 (3), p.427-432 [Periódico revisado por pares]

United States: Nature Publishing Group

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