Allele-specific RNA silencing of mutant ataxin-3 mediates neuroprotection in a rat model of Machado-Joseph disease

Alves, Sandro ; Nascimento-Ferreira, Isabel ; Auregan, Gwennaëlle ; Hassig, Raymonde ; Dufour, Noëlle ; Brouillet, Emmanuel ; Pedroso de Lima, Maria C ; Hantraye, Philippe ; Pereira de Almeida, Luís ; Déglon, Nicole Cookson, Mark R.

PloS one, 2008-10, Vol.3 (10), p.e3341-e3341 [Periódico revisado por pares]

United States: Public Library of Science

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