Enzyme replacement therapy for mucopolysaccharidosis VI: A phase 3, randomized, double-blind, placebo-controlled, multinational study of recombinant human N-acetylgalactosamine 4-sulfatase (recombinant human arylsulfatase B or rhASB) and follow-on, open-label extension study

Harmatz, Paul ; Giugliani, Roberto ; Schwartz, Ida ; Guffon, Nathalie ; Teles, Elisa Leão ; Miranda, M. Clara Sá ; Wraith, J. Edmond ; Beck, Michael ; Arash, Laila ; Scarpa, Maurizio ; Yu, Zi-Fan ; Wittes, Janet ; Berger, Kenneth I. ; Newman, Mary S. ; Lowe, Ann M. ; Kakkis, Emil ; Swiedler, Stuart J.

The Journal of pediatrics, 2006-04, Vol.148 (4), p.533-539.e6 [Periódico revisado por pares]

New York, NY: Mosby, Inc

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