Peripheral transvenular delivery of adeno-associated viral vectors to skeletal muscle as a novel therapy for hemophilia B

Arruda, Valder R. ; Stedman, Hansell H. ; Haurigot, Virginia ; Buchlis, George ; Baila, Stefano ; Favaro, Patricia ; Chen, Yifeng ; Franck, Helen G. ; Zhou, Shangzhen ; Wright, J. Fraser ; Couto, Linda B. ; Jiang, Haiyan ; Pierce, Glenn F. ; Bellinger, Dwight A. ; Mingozzi, Federico ; Nichols, Timothy C. ; High, Katherine A.

Blood, 2010-06, Vol.115 (23), p.4678-4688 [Periódico revisado por pares]

Washington, DC: Elsevier Inc

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