Nonclinical Safety Evaluation of scAAV8- RLBP1 for Treatment of RLBP1 Retinitis Pigmentosa

MacLachlan, Timothy K ; Milton, Mark N ; Turner, Oliver ; Tukov, Francis ; Choi, Vivian W ; Penraat, Jan ; Delmotte, Marie-Hélène ; Michaut, Lydia ; Jaffee, Bruce D ; Bigelow, Chad E

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United States: Elsevier Limited

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