2-Year Change in Revised Hammersmith Scale Scores in a Large Cohort of Untreated Paediatric Type 2 and 3 SMA Participants

Stimpson, Georgia ; Ramsey, Danielle ; Wolfe, Amy ; Mayhew, Anna ; Scoto, Mariacristina ; Baranello, Giovanni ; Muni Lofra, Robert ; Main, Marion ; Milev, Evelin ; Coratti, Giorgia ; Pane, Marika ; Sansone, Valeria ; D'Amico, Adele ; Bertini, Enrico ; Messina, Sonia ; Bruno, Claudio ; Albamonte, Emilio ; Mazzone, Elena Stacy ; Montes, Jacqueline ; Glanzman, Allan M ; Zolkipli-Cunningham, Zarazuela ; Pasternak, Amy ; Duong, Tina ; Dunaway Young, Sally ; Civitello, Matthew ; Marini-Bettolo, Chiara ; Day, John W ; Darras, Basil T ; De Vivo, Darryl C ; Finkel, Richard S ; Mercuri, Eugenio ; Muntoni, Francesco

Journal of clinical medicine, 2023-02, Vol.12 (5), p.1920 [Periódico revisado por pares]

Switzerland: MDPI AG

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