PMP22 antisense oligonucleotides reverse Charcot-Marie-Tooth disease type 1A features in rodent models

Zhao, Hien Tran ; Damle, Sagar ; Ikeda-Lee, Karli ; Kuntz, Steven ; Li, Jian ; Mohan, Apoorva ; Kim, Aneeza ; Hung, Gene ; Scheideler, Mark A ; Scherer, Steven S ; Svaren, John ; Swayze, Eric E ; Kordasiewicz, Holly B

The Journal of clinical investigation, 2018-01, Vol.128 (1), p.359-368 [Periódico revisado por pares]

United States: American Society for Clinical Investigation

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