Intravenous administration of brain-targeted stable nucleic acid lipid particles alleviates Machado-Joseph disease neurological phenotype
Conceição, Mariana ; Mendonça, Liliana ; Nóbrega, Clévio ; Gomes, Célia ; Costa, Pedro ; Hirai, Hirokazu ; Moreira, João Nuno ; Lima, Maria C ; Manjunath, N ; Pereira de Almeida, Luís
Biomaterials, 2016-03, Vol.82, p.124-137 [Periódico revisado por pares]Netherlands: Elsevier Ltd
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