Pivotal trial with plant cell–expressed recombinant glucocerebrosidase, taliglucerase alfa, a novel enzyme replacement therapy for Gaucher disease

Zimran, Ari ; Brill-Almon, Einat ; Chertkoff, Raul ; Petakov, Milan ; Blanco-Favela, Francisco ; Muñoz, Eduardo Terreros ; Solorio-Meza, Sergio E. ; Amato, Dominick ; Duran, Gloria ; Giona, Fiorina ; Heitner, Rene ; Rosenbaum, Hanna ; Giraldo, Pilar ; Mehta, Atul ; Park, Glen ; Phillips, Mici ; Elstein, Deborah ; Altarescu, Gheona ; Szleifer, Mali ; Hashmueli, Sharon ; Aviezer, David

Blood, 2011-11, Vol.118 (22), p.5767-5773 [Periódico revisado por pares]

Washington, DC: Elsevier Inc

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