A Universal Approach to Correct Various HBB Gene Mutations in Human Stem Cells for Gene Therapy of Beta‐Thalassemia and Sickle Cell Disease

Cai, Liuhong ; Bai, Hao ; Mahairaki, Vasiliki ; Gao, Yongxing ; He, Chaoxia ; Wen, Yanfei ; Jin, You‐Chuan ; Wang, You ; Pan, Rachel L. ; Qasba, Armaan ; Ye, Zhaohui ; Cheng, Linzhao

Stem cells translational medicine, 2018-01, Vol.7 (1), p.87-97 [Periódico revisado por pares]

United States: Oxford University Press

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