In vivo genome editing of the albumin locus as a platform for protein replacement therapy

Sharma, Rajiv ; Anguela, Xavier M. ; Doyon, Yannick ; Wechsler, Thomas ; DeKelver, Russell C. ; Sproul, Scott ; Paschon, David E. ; Miller, Jeffrey C. ; Davidson, Robert J. ; Shivak, David ; Zhou, Shangzhen ; Rieders, Julianne ; Gregory, Philip D. ; Holmes, Michael C. ; Rebar, Edward J. ; High, Katherine A.

Blood, 2015-10, Vol.126 (15), p.1777-1784 [Periódico revisado por pares]

United States: Elsevier Inc

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