Result Number | Material Type | Add to My Shelf Action | Record Details and Options |
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1 |
Material Type: Artigo
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Author IndexMolecular therapy, 2006-05, Vol.13 (S1), p.S430 [Periódico revisado por pares]Milwaukee: Elsevier LimitedTexto completo disponível |
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2 |
Material Type: Artigo
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Author IndexMolecular therapy, 2008-05, Vol.16 (1s), p.S390 [Periódico revisado por pares]Milwaukee: Elsevier LimitedTexto completo disponível |
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3 |
Material Type: Artigo
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Author IndexMolecular therapy, 2009-05, Vol.17 (S1), p.S397 [Periódico revisado por pares]Milwaukee: Elsevier LimitedTexto completo disponível |
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4 |
Material Type: Artigo
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Lack of Immunotoxicity After Regional Intravenous (RI) Delivery of rAAV to Nonhuman Primate Skeletal MuscleToromanoff, Alice ; Adjali, Oumeya ; Larcher, Thibaut ; Hill, Marcelo ; Guigand, Lydie ; Chenuaud, Pierre ; Deschamps, Jack-Yves ; Gauthier, Olivier ; Blancho, Gilles ; Vanhove, Bernard ; Rolling, Fabienne ; Chérel, Yan ; Moullier, Philippe ; Anegon, Ignacio ; Le Guiner, CarolineMolecular therapy, 2010-01, Vol.18 (1), p.151-160 [Periódico revisado por pares]United States: Elsevier IncTexto completo disponível |
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5 |
Material Type: Artigo
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Author IndexMolecular therapy, 2010-05, Vol.18 (Supplement 1), p.S353 [Periódico revisado por pares]Milwaukee: Elsevier LimitedTexto completo disponível |
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6 |
Material Type: Artigo
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Author IndexMolecular therapy, 2011-05, Vol.19 (Supplement 1), p.S333 [Periódico revisado por pares]Milwaukee: Elsevier LimitedTexto completo disponível |
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7 |
Material Type: Artigo
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Author IndexMolecular therapy, 2012-05, Vol.20 (Supplement 1), p.S295 [Periódico revisado por pares]Milwaukee: Elsevier LimitedTexto completo disponível |
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8 |
Material Type: Artigo
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Engineering Multiple U7snRNA Constructs to Induce Single and Multiexon-skipping for Duchenne Muscular DystrophyGoyenvalle, Aurélie ; Wright, Jordan ; Babbs, Arran ; Wilkins, Vivienne ; Garcia, Luis ; Davies, Kay EMolecular therapy, 2012-06, Vol.20 (6), p.1212-1221 [Periódico revisado por pares]United States: Elsevier IncTexto completo disponível |
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9 |
Material Type: Artigo
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Converting Pathological Cells to Therapeutic Ones: An Odyssey Through PluripotencyVilquin, Jean-ThomasMolecular therapy, 2012-11, Vol.20 (11), p.2012-2014 [Periódico revisado por pares]United States: Elsevier IncTexto completo disponível |
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10 |
Material Type: Artigo
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Muscle Function Recovery in Golden Retriever Muscular Dystrophy After AAV1-U7 Exon SkippingVulin, Adeline ; Barthélémy, Inès ; Goyenvalle, Aurélie ; Thibaud, Jean-Laurent ; Beley, Cyriaque ; Griffith, Graziella ; Benchaouir, Rachid ; le Hir, Maëva ; Unterfinger, Yves ; Lorain, Stéphanie ; Dreyfus, Patrick ; Voit, Thomas ; Carlier, Pierre ; Blot, Stéphane ; Garcia, LuisMolecular therapy, 2012-11, Vol.20 (11), p.2120-2133 [Periódico revisado por pares]United States: Elsevier IncTexto completo disponível |