Levels of Anti-FVIII IgG4 and Total IgG Are Biomarkers of Immune Tolerance Induction Failure in Patients with Inherited Hemophilia a and High-Responding Inhibitors

Rezende, Suely Meireles ; Ayala, Brendon ; Camelo, Ricardo ; Dias, Maise M. ; Oliveira, Andrea G. ; Franco, Vivian K. B. ; Cerqueira, Monica H. ; Lorenzato, Claudia S. ; Ribeiro, Rosangela A. ; Callado, Fábia M. R. A. ; Cerqueira, Maria Aline ; Etto, Leina Y. ; Roberti, Maria do Rosário ; Anegawa, Tânia H. ; Pinto, Ieda ; Gonçalves Chaves, Daniel

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Factor B Inhibition with Oral Iptacopan Monotherapy Demonstrates Sustained Long-Term Efficacy and Safety in Anti-C5-Treated Patients (pts) with Paroxysmal Nocturnal Hemoglobinuria (PNH) and Persistent Anemia: Final 48-Week Results from the Multicenter, Phase III APPLY-PNH Trial

Risitano, Antonio M ; Kulasekararaj, Austin ; Roeth, Alexander ; Scheinberg, Phillip ; Ueda, Yasutaka ; de Castro, Carlos ; Di Bona, Eros ; Griffin, Morag ; Langemeijer, Saskia MC ; Schrezenmeier, Hubert ; Barcellini, Wilma ; Mauad, Vitor AQ ; Panse, Jens ; Schafhausen, Philippe ; Tavitian, Suzanne ; Beggiato, Eloise ; Gaya, Anna ; Huang, Wei-Han ; Kitawaki, Toshio ; Kutlar, Abdullah ; Maciejewski, Jaroslaw P. ; Notaro, Rosario ; Pullarkat, Vinod ; Schubert, Jörg ; Terriou, Louis ; Uchiyama, Michihiro ; Sicre De Fontbrune, Flore ; Frieri, Camilla ; Alashkar, Ferras ; Gandhi, Shreyans ; Kumar, Rakesh ; Thorburn, Christine ; Maitra, Samopriyo ; Solar-Yohay, Susan ; Lawniczek, Tomasz ; Dahlke, Marion ; Peffault De Latour, Régis

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SF3B1, RUNX1 and TP53 Mutations Significantly Impact the Outcome of Patients with Lower-Risk Myelodysplastic Syndrome

Falantes, Jose F. ; Márquez-Malaver, Francisco J. ; Carrillo-Cruz, Estrella ; Morales-Camacho, Rosario M ; Prats-Martín, Concepción ; Caballero, Teresa ; Rodriguez Arbolí, Eduardo ; Espigado, Ildefonso ; Perez-Simon, Jose A.

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Role of Allogeneic Hematopoietic Cell Transplant for Relapsed/Refractory Large B-Cell Lymphomas in the CART Era

Mussetti, Alberto ; Bento, Leyre ; Bastos-Oreiro, Mariana ; Albo, Carmen ; Bailen, Rebeca ; Barba, Pere ; Benzaquén, Ana ; Briones, Javier ; Caballero, Ana Carolina ; Campos, António ; Español, Ignacio ; Ferra, Christelle ; Garzón López, Sebastián ; González Sierra, Pedro Antonio ; Guerra, Luisa Maria ; Hernani, Rafael ; Iacoboni, Gloria ; Jiminez Ubieto, Ana Isabel ; Kwon, Mi ; López Corral, Lucía ; López-Godino, Oriana ; Martinez Munoz, Maria Carmen ; Martínez-Cibrián, Nuria ; Montoro Gómez, Juan ; Pérez-Ortega, Laura ; Ortí, Guillermo ; Ortiz-Maldonado, Valentín ; Pascual, Maria-Jesús ; Perera, María ; Perez, Antonio ; Reguera, Juan Luis ; Sanchez, Jose M. ; Sanz, Jaime ; Torrent, Anna ; Yáñez, Lucrecia ; Varela, Rosario ; Ceberio Echechipia, Izaksun ; Caballero, Dolores ; Sureda, Anna

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Autosomal Recessive Congenital Dyserythropoietic Anemia Type III Is Caused By Mutations in the Centralspindlin RACGAP1 Component

Romero-Cortadellas, Lídia ; Hernández, Gonzalo ; Ferrer-Cortès, Xènia ; Venturi, Veronica ; Olivella, Mireia ; Pérez de Soto, Concepción ; Morales-Camacho, Rosario M. ; Villegas, Ana ; Gonzalez-Fernandez, F. Ataulfo ; Morado, Marta ; Pérez-Montero, Santiago ; Tornador, Cristian ; Sánchez, Mayka

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Phase 2 study of danicopan in patients with paroxysmal nocturnal hemoglobinuria with an inadequate response to eculizumab

Kulasekararaj, Austin G. ; Risitano, Antonio M. ; Maciejewski, Jaroslaw P. ; Notaro, Rosario ; Browett, Peter ; Lee, Jong Wook ; Huang, Mingjun ; Geffner, Michael ; Brodsky, Robert A.

United States: Elsevier Inc

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Frequency, Clinical Characteristics and Outcome of Adult Patients with Acute Lymphoblastic Leukemia (ALL) and COVID-19 in Spain: Results of a Survey from Pethema and Geth Groups

Ribera, Josep-Maria ; Morgades, Mireia ; Coll, Rosa ; Lopez Lorenzo, Jose Luis ; Montesinos, Pau ; Varela, Rosario ; Cabrero, Mónica ; Gómez-Centurión, Ignacio ; Morales, M. Dolores ; Garcia-Guiñon, Antoni ; Bautista, Guiomar ; Herrera Puente, Pilar ; Llorente, Laura ; García-Cadenas, Irene ; Barba, Pere ; Calbacho, Maria ; Gil, Cristina ; Foncillas, Maria Angeles ; Artola, María Teresa ; De La Camara, Rafael ; Piñana Sanchez, Jose Luis

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Allogeneic Hematopoietic Stem Cell Transplantation for T Cell Lymphomas: Improved Results Overtime

Novelli, Silvana ; Bento, Leyre ; García-Cadenas, Irene ; Prieto, Laura ; Corral, Lucía López ; Gutierrez Garcia, Gonzalo ; Hernani, Rafael ; Pérez Martínez, Ariadna ; Sierra, Jorge ; Solano, Carlos ; Bastos-Oreiro, Mariana ; Dorado, Nieves ; Rodríguez-Torres, Nancy ; Rodríguez, Guillermo ; Piñana Sanchez, Jose Luis ; Montoro Gómez, Juan ; Herrera Puente, Pilar ; Luna, Alejandro ; Sanchez Ortega, Isabel ; Martin Calvo, Carmen ; López-Godino, Oriana ; Heras, Inmaculada ; Zanabili, Joud ; Palomo Moraleda, María Del Pilar ; Parody, Rocio ; Moraleda, Jose Maria ; Yáñez, Lucrecia ; Gutiérrez, Antonio ; Zudaire, Teresa ; Cordoba, Raul ; Varela, Rosario ; Ferra, Christelle M ; Martinez-Lopez, Joaquin ; García-Torres, Estefania ; Caballero, Dolores

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A Phase 2 Open-Label Study of Danicopan (ACH-0144471) in Patients with Paroxysmal Nocturnal Hemoglobinuria (PNH) Who Have an Inadequate Response to Eculizumab Monotherapy

Kulasekararaj, Austin ; Risitano, Antonio M. ; Maciejewski, Jaroslaw P. ; Notaro, Rosario ; Browett, Peter ; Lee, Jong-Wook ; Huang, Mingjun ; Geffner, Michael ; Brodsky, Robert A.

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Mechanistic Evaluation of Efficacy Using Biomarkers of the Oral, Small Molecule Factor D Inhibitor, Danicopan (ACH-4471), in Untreated Patients with Paroxysmal Nocturnal Hemoglobinuria (PNH)

Risitano, Antonio M. ; Lee, Jong Wook ; Notaro, Rosario ; Brodsky, Robert A. ; Kulasekararaj, Austin ; Maciejewski, Jaroslaw P. ; Huang, Mingjun ; Geffner, Michael ; Browett, Peter

Elsevier Inc

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