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1 |
Material Type: Artigo
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Highly Aligned Ternary Nanofiber Matrices Loaded with MXene Expedite Regeneration of Volumetric Muscle LossKang, Moon Sung ; Yu, Yeuni ; Park, Rowoon ; Heo, Hye Jin ; Lee, Seok Hyun ; Hong, Suck Won ; Kim, Yun Hak ; Han, Dong-WookNano-micro letters, 2024-12, Vol.16 (1), p.73-73, Article 73 [Periódico revisado por pares]Singapore: Springer Nature SingaporeTexto completo disponível |
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Material Type: Artigo
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Petrosamine isolated from marine sponge Petrosia sp. demonstrates protection against neurotoxicity in vitro and in vivoRibeiro, Joana ; Araújo-Silva, Henrique ; Fernandes, Mário ; da Silva, Joilna Alves ; Pinto, Francisco das Chagas L. ; Pessoa, Otília Deusdenia L. ; Santos, Hélcio Silva ; de Menezes, Jane Eire Silva Alencar ; Gomes, Andreia C.Natural products and bioprospecting, 2024-12, Vol.14 (1), p.16-16, Article 16 [Periódico revisado por pares]Singapore: Springer Nature SingaporeTexto completo disponível |
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Material Type: Artigo
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Targeting miR-25 to alleviate DMD-related muscle dysfunctionLi, Shuang ; Han, RenzhiMolecular therapy. Nucleic acids, 2024-09, Vol.35 (3), p.102238, Article 102238 [Periódico revisado por pares]Elsevier IncTexto completo disponível |
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Material Type: Artigo
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miR-181a, delivered by hypoxic PTC-secreted exosomes, inhibits DACT2 by downregulating MLL3, leading to YAP-VEGF-mediated angiogenesisWang, Yingxue ; Cen, Aiying ; Yang, Yuxian ; Ye, Huilin ; Li, Jiaying ; Liu, Shiliang ; Zhao, LeiMolecular therapy. Nucleic acids, 2024-09, Vol.35 (3), p.102239, Article 102239 [Periódico revisado por pares]Elsevier IncTexto completo disponível |
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Material Type: Artigo
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A novel multitargeted self-assembling peptide-siRNA complex for simultaneous inhibition of SARS-CoV-2-host cell interaction and replicationTuttolomondo, Martina ; Pham, Stephanie Thuy Duong ; Terp, Mikkel Green ; Cendán Castillo, Virginia ; Kalisi, Nazmie ; Vogel, Stefan ; Langkjær, Niels ; Hansen, Ulla Melchior ; Thisgaard, Helge ; Schrøder, Henrik Daa ; Palarasah, Yaseelan ; Ditzel, Henrik JørnMolecular therapy. Nucleic acids, 2024-09, Vol.35 (3), p.102227, Article 102227 [Periódico revisado por pares]Elsevier IncTexto completo disponível |
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Material Type: Artigo
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Harnessing mRNA to unleash endolysins: A new frontier in antibacterial therapyNelson, Daniel C. ; Dave, Urmil M. ; Gonzalez-Juarbe, NorbertoMolecular therapy. Nucleic acids, 2024-09, Vol.35 (3), p.102249, Article 102249 [Periódico revisado por pares]Elsevier IncTexto completo disponível |
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Material Type: Artigo
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Extracellular vesicle transfer of lncRNA H19 splice variants to cardiac cellsVilaça, Andreia ; Jesus, Carlos ; Lino, Miguel ; Hayman, Danika ; Emanueli, Costanza ; Terracciano, Cesare M. ; Fernandes, Hugo ; de Windt, Leon J. ; Ferreira, LinoMolecular therapy. Nucleic acids, 2024-09, Vol.35 (3), p.102233, Article 102233 [Periódico revisado por pares]Elsevier IncTexto completo disponível |
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Material Type: Artigo
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CircHTT(2,3,4,5,6)— co-evolving with the HTT CAG-repeat tract — modulates Huntington's disease phenotypesMorandell, Jasmin ; Monziani, Alan ; Lazioli, Martina ; Donzel, Deborah ; Döring, Jessica ; Oss Pegorar, Claudio ; D’Anzi, Angela ; Pellegrini, Miguel ; Mattiello, Andrea ; Bortolotti, Dalia ; Bergonzoni, Guendalina ; Tripathi, Takshashila ; Mattis, Virginia B. ; Kovalenko, Marina ; Rosati, Jessica ; Dieterich, Christoph ; Dassi, Erik ; Wheeler, Vanessa C. ; Ellederová, Zdenka ; Wilusz, Jeremy E. ; Viero, Gabriella ; Biagioli, MartaMolecular therapy. Nucleic acids, 2024-09, Vol.35 (3), p.102234, Article 102234 [Periódico revisado por pares]Elsevier IncTexto completo disponível |
9 |
Material Type: Artigo
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Upregulation of utrophin improves the phenotype of Duchenne muscular dystrophy hiPSC-derived CMsAndrysiak, Kalina ; Ferdek, Paweł E. ; Sanetra, Anna M. ; Machaj, Gabriela ; Schmidt, Luisa ; Kraszewska, Izabela ; Sarad, Katarzyna ; Palus-Chramiec, Katarzyna ; Lis, Olga ; Targosz-Korecka, Marta ; Krüger, Marcus ; Lewandowski, Marian H. ; Ylla, Guillem ; Stępniewski, Jacek ; Dulak, JózefMolecular therapy. Nucleic acids, 2024-09, Vol.35 (3), p.102247, Article 102247 [Periódico revisado por pares]Elsevier IncTexto completo disponível |
10 |
Material Type: Artigo
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Preclinical evaluation of stereopure antisense oligonucleotides for allele-selective lowering of mutant HTTIwamoto, Naoki ; Liu, Yuanjing ; Frank-Kamenetsky, Maria ; Maguire, Abbie ; Tseng, Wei Chou ; Taborn, Kristin ; Kothari, Nayantara ; Akhtar, Ali ; Bowman, Keith ; Shelke, Juili Dilip ; Lamattina, Anthony ; Hu, Xiao Shelley ; Jang, Hyun Gyung ; Kandasamy, Pachamuthu ; Liu, Fangjun ; Longo, Ken ; Looby, Richard ; Meena ; Metterville, Jake ; Pan, Qianli ; Purcell-Estabrook, Erin ; Shimizu, Mamoru ; Prakasha, Priyanka Shiva ; Standley, Stephany ; Upadhyay, Hansini ; Yang, Hailin ; Yin, Yuan ; Zhao, Anderson ; Francis, Christopher ; Byrne, Mike ; Dale, Elena ; Verdine, Gregory L. ; Vargeese, ChandraMolecular therapy. Nucleic acids, 2024-09, Vol.35 (3), p.102246, Article 102246 [Periódico revisado por pares]Elsevier IncTexto completo disponível |